0
Skip to Content
RUNX1 Research Program
RUNX1 Research Program
For Patients
For Researchers
For Clinicians
Take Action
About Us
English
DONATE
RUNX1 Research Program
RUNX1 Research Program
For Patients
For Researchers
For Clinicians
Take Action
About Us
English
DONATE
For Patients
For Researchers
For Clinicians
Take Action
About Us
English
Back
DONATE
  • Patient Videos & Webinars,
• 8/7/24

Module 3: The Potential Promise and Current Challenges of Gene Editing

This module explores advanced gene editing techniques like CRISPR to correct stem cells outside of the body in order to transform 'blue' problematic stem cells into 'green' healthy ones.

It also highlights why current techniques aren’t safe enough for a RUNX1-FPD gene therapy yet.

Previous

Module 2: The Therapeutic Potential of Increasing RUNX1 Activity Using a Drug

Next

Module 4: Banking Stem Cells Today for the Possible Gene Editing Capabilities of Tomorrow

You Might Also Like

Related Embedded Video Item Thumbnail Interface guided phenotyping of coding variants in the transcription factor RUNX1 with SEUSS
Related Embedded Video Item Thumbnail Mutation-Specific Epigenetic Reprogramming of Hematopoietic Stem Cells in AML
Related Embedded Video Item Thumbnail RUNX1 Patient Data Hub Demo 3: Patient Tools
Related Embedded Video Item Thumbnail Neoplasias Hematológicas Hereditarias: No Tan Poco Frecuentes (September 2024)
Related Embedded Video Item Thumbnail RRP Patient Meeting 2023: RUNX1 PDH Update Nov 2023 - Dr. Amanda Eggen, RRP

Sign Up For Our Email List!

Enter your information below to receive the
latest RUNX1 news and updates!

Stay In Touch

Email RRP

Newsletter

Policies

Privacy Policy

Cookie Policy

Accessibility Statement

Site Resources

News & Updates

Calendar of Events

RRP Blog

DONATE
SHOP