In the first half of this webinar, study lead Dr. Courtney DiNardo from MD Anderson Cancer Center provides an overview of the Low-Dose Sirolimus Pilot Study for RUNX1-FPD.

Topics covered include:

• The scientific rationale for using sirolimus in RUNX1-FPD

• Study design, eligibility, and objectives

• Early observations from pilot study participants This session was designed for RUNX1-FPD patients, families, and anyone interested in understanding sirolimus as a potential treatment option.

Full video: https://youtu.be/rH-niYhREuI

Part 2 (Patients only): https://youtu.be/WhlWTV_snkY